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Pipeline

A Broad Pipeline Approaching the Clinic

Using a delivery-centric approach to unlock the power of genetic medicines across many disease areas.

Program
Discovery
Lead Optimization
IND Enabling
Clinical Development
Targeted LNPs

AERA-109: Targeted In Vivo CAR-T for Autoimmune Disease

mid IND Enabling phase

Next Gen Targeted LNP Programs

Discovery phase
Antibody-Oligo Conjugates

Cardiac Targeted AOC

Lead Optimization Phase

Other Muscle
Targeted AOC

Discovery phase
Protein Nano-Particles

CNS Targeted PNP

Discovery phase

Targeted LNPs

AERA-109: Targeted In Vivo CAR-T for Autoimmune Disease

Discovery
Lead Optimization
IND Enabling
Clinical Development
mid IND Enabling phase

Next Gen Targeted LNP Programs

Discovery
Lead Optimization
IND Enabling
Clinical Development
Discovery phase

Antibody-Oligo Conjugates

Cardiac Targeted AOC

Discovery
Lead Optimization
IND Enabling
Clinical Development
Lead Optimization Phase

Other Muscle
Targeted AOC

Discovery
Lead Optimization
IND Enabling
Clinical Development
Discovery phase

Protein Nano-Particles

CNS Targeted PNP

Discovery
Lead Optimization
IND Enabling
Clinical Development
Discovery phase
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